Claudio L Santos

Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry.

E. Mercuri, F. Muntoni, I. Desguerre, 2019, Journal of comparative effectiveness research.

Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study

E. Mercuri, F. Muntoni, I. Desguerre, 2020, Journal of comparative effectiveness research.

Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy.

S. Peltz, S. Apkon, C. Campbell, 2021, Journal of comparative effectiveness research.