C. Smith

发表

Extracellular vesicle in vivo biodistribution is determined by cell source, route of administration and targeting

Imre Mäger, Pieter Vader, Ylva Gustafsson, 2015, Journal of extracellular vesicles.

Intercellular delivery of thymidine kinase prodrug activating enzyme by the herpes simplex virus protein, VP22

A. Phelan, A. Aints, M. Dilber, 1999, Gene Therapy.

Multi-level omics analysis in a murine model of dystrophin loss and therapeutic restoration

C. I. Smith, M. Wood, J. Lehtiö, 2015, Human molecular genetics.

Oligonucleotide Therapies: The Past and the Present

M. Behlke, K. E. Lundin, C. Smith, 2015, Human gene therapy.

Cells release subpopulations of exosomes with distinct molecular and biological properties

Henrik J Johansson, Janne Lehtiö, Imre Mäger, 2016, Scientific Reports.

A Peptide-based Vector for Efficient Gene Transfer In Vitro and In Vivo.

P. Lundin, I. Mäger, S. E. Andaloussi, 2011, Molecular therapy : the journal of the American Society of Gene Therapy.

Lipid-based Transfection Reagents Exhibit Cryo-induced Increase in Transfection Efficiency

R. Schiffelers, M. Wood, M. Pooga, 2016, Molecular Therapy: Nucleic Acids.

Agammaglobulinemia: causative mutations and their implications for novel therapies

O. Gissberg, Burcu Bestas, K. Blomberg, 2013, Expert review of clinical immunology.

Micro-minicircle Gene Therapy: Implications of Size on Fermentation, Complexation, Shearing Resistance, and Expression

K. E. Lundin, M. Rutland, B. Wahrén, 2014, Molecular therapy. Nucleic acids.

Solid formulation of cell-penetrating peptide nanocomplexes with siRNA and their stability in simulated gastric conditions

C. I. Smith, Ü. Langel, S. El Andaloussi, 2012, Journal of Controlled Release.

Transcriptional signatures of Itk-deficient CD3+, CD4+ and CD8+ T-cells

Jessica M. Lindvall, W. Ellmeier, K. Blomberg, 2009, BMC Genomics.

CTG repeat-targeting oligonucleotides for down-regulating Huntingtin expression

K. E. Lundin, J. Wengel, R. Zain, 2017, Nucleic acids research.

Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides

Ashley M. Jacobi, M. Behlke, S. Hammond, 2014, Molecular therapy. Nucleic acids.

Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides.

Ashley M. Jacobi, M. Behlke, S. Hammond, 2014, Molecular therapy. Nucleic acids.

Peptide Nanoparticle Delivery of Charge-Neutral Splice-Switching Morpholino Oligonucleotides

S. Hammond, M. Wood, M. Hällbrink, 2015, Nucleic acid therapeutics.

Non-viral nanovectors for gene delivery: factors that govern successful therapeutics

S. El-Andaloussi, J. Viola, I. Oprea, 2010, Expert opinion on drug delivery.

In vivo nuclear delivery of oligonucleotides via hybridizing bifunctional peptides

L. Branden, B. Christensson, C. Smith, 2001, Gene Therapy.

Translocation-generated ITK-FER and ITK-SYK fusions induce STAT3 phosphorylation and CD69 expression.

R. Zain, A. Görgens, B. Nore, 2018, Biochemical and biophysical research communications.

Novel peptide‐dendrimer/lipid/oligonucleotide ternary complexes for efficient cellular uptake and improved splice‐switching activity

J. Reymond, F. Hollfelder, K. E. Lundin, 2018, European journal of pharmaceutics and biopharmaceutics : official journal of Arbeitsgemeinschaft fur Pharmazeutische Verfahrenstechnik e.V.

Eleven percent intact PGM3 in a severely immunodeficient patient with a novel splice-site mutation, a case report

K. E. Lundin, A. Wikström, P. Marits, 2018, BMC Pediatrics.

Susceptibility to infections, without concomitant hyper-IgE, reported in 1976, is caused by hypomorphic mutation in the phosphoglucomutase 3 (PGM3) gene

L. Moens, K. E. Lundin, M. Bjørås, 2015, Clinical immunology.

Circular RNA interference effector molecules (WO10084371)

P. Lundin, P. Moreno, S. Andaloussi, 2011, Expert opinion on therapeutic patents.

Growth Media Conditions Influence the Secretion Route and Release Levels of Engineered Extracellular Vesicles

R. Zain, Dhanu Gupta, Jeremy P Bost, 2021, Advanced healthcare materials.

Suicide genes and bystander killing: local and distant effects

M. Dilber, C. Smith, 1997, Gene Therapy.

Biological activity and biotechnological aspects of locked nucleic acids.

J. Kjems, K. E. Lundin, J. Wengel, 2013, Advances in genetics.

Information to : A nuclease resistant oligonucleotide with cell penetrating properties

C. I. Smith, R. Strömberg, Cristina S. J. Rocha, 2015 .

Proximal promoter of the murine syndecan‐1 gene is not sufficient for the developmental pattern of syndecan expression in B lineage cells

G. Gahrton, P. Jaakkola, M. Jalkanen, 2001, American journal of hematology.

Design and application of bispecific splice-switching oligonucleotides.

C. I. Smith, S. Hammond, M. Wood, 2014, Nucleic acid therapeutics.