M. Hale

Long-term open-label extension study of the safety and efficacy of intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II.

B. Burton, M. Inbar‐Feigenberg, J. Muenzer, 2022, Molecular genetics and metabolism.

Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study.

B. Burton, M. Inbar‐Feigenberg, J. Muenzer, 2022, Molecular genetics and metabolism.

A randomized double-blind, multicenter plasma concentration controlled study of the safety and efficacy of oral mycophenolate mofetil for the prevention of acute rejection after kidney transplantation.

J. Squifflet, J. D. de Fijter, W. Weimar, 1998, Transplantation.