M. Giorgi

Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice.

E. Payen, P. Leboulch, K. Sii-Felice, 2018, Experimental hematology.

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

M. Denaro, S. Borwornpinyo, P. Leboulch, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia

J. Vadolas, S. Fucharoen, G. Grigoriadis, 2021, Molecular therapy : the journal of the American Society of Gene Therapy.

Towards the Clinical Application of Gene Therapy for Genetic Inner Ear Diseases

S. Safieddine, M. Lecomte, G. Lahlou, 2023, Journal of clinical medicine.

P. FAGGIOLI1, E. ZACCARA1, L. CASTELNOVO1, D. BOMPANE1, A. TAMBURELLO1, A. LURATI1, A. LARIA1, D. GANGEMI2, M. GIANI2, D. GNANI2, M. DI GIORGI2, K. IURA2, F. GRANDELIS2, R. PIAZZA3, T. PIANA4, G. ZIZZO1, A. MAZZONE5

G. Zizzo, A. Lurati, D. Bompane, 2023 .