Luis Felipe Marinho

Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector

W. Hauswirth, A. Cideciyan, S. Jacobson, 2018, Proceedings of the National Academy of Sciences.

Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations.

Paul D. Gamlin, W. Hauswirth, A. Cideciyan, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.

Overlap of abnormal photoreceptor development and progressive degeneration in Leber congenital amaurosis caused by NPHP5 mutation.

A. Cideciyan, S. Jacobson, G. Aguirre, 2016, Human molecular genetics.

Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations.

Paul D. Gamlin, W. Hauswirth, A. Cideciyan, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.