E. Fratini

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

V. Gallo, P. Rancoita, C. Di Serio, 2022, The Lancet.

Emapalumab treatment in an ADA-SCID patient with refractory hemophagocytic lymphohistiocytosis- related graft failure and disseminated bacillus Calmette-Guérin infection

V. Gallo, C. Baldoli, A. Aiuti, 2020, Haematologica.

Hemophagocytic inflammatory syndrome in ADA-SCID: report of two cases and literature review

V. Gallo, M. Duse, M. Bernardo, 2023, Frontiers in Immunology.

Mild SARS-CoV-2 Infection After Gene Therapy in a Child With Wiskott-Aldrich Syndrome: A Case Report

V. Gallo, L. Piemonti, A. Aiuti, 2020, Frontiers in Immunology.

Lentiviral hematopoietic stem and progenitor cell gene therapy provides durable clinical benefit in early-symptomatic early-juvenile metachromatic leukodystrophy

M. Filippi, V. Gallo, L. Naldini, 2021 .