P. Frattini

Autologous intramuscular transplantation of engineered satellite cells induces exosome-mediated systemic expression of Fukutin-related protein and rescues disease phenotype in a murine model of limb-girdle muscular dystrophy type 2I

M. Raimondi, C. Villa, S. Erratico, 2017, Human molecular genetics.

Stem Cell-Mediated Exon Skipping of the Dystrophin Gene by the Bystander Effect.

A. Tavelli, M. Belicchi, Y. Torrente, 2015, Current gene therapy.