N. Cornell

Variation in Transfusion Requirements Among Children With Thalassemia on Regular Transfusion Programs: Which Formula Closely Predicts the Actual Requirements?

M. Eisenhut, S. Ramprakash, N. Cornell, 2017, Journal of pediatric hematology/oncology.

Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain

M. Scoto, E. Wraige, D. Parasuraman, 2024, Journal of neuromuscular diseases.