M. McIntyre

Protein Phosphatase Inhibitor-1 Gene Therapy in a Swine Model of Nonischemic Heart Failure.

R. Samulski, T. Weber, R. Hajjar, 2017, Journal of the American College of Cardiology.

Not reinventing the wheel: applying the 3Rs concepts to viral vector gene therapy biodistribution studies.

T. Maclachlan, K. Mitrophanous, D. Jolly, 2013, Human gene therapy. Clinical development.

Investigational new drugs submitted to the Food and Drug Administration that are placed on clinical hold: the experience of the Office of Cellular, Tissue and Gene Therapy.

S. Hirschfeld, K. Wonnacott, R. Fiorentino, 2008, Cytotherapy.

Biodistribution studies: understanding international expectations

Leelee Ong, A. Kume, N. Ferry, 2016, Molecular Therapy. Methods & Clinical Development.

Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy

J. Grieger, T. Larcher, Juan Li, 2023, Molecular therapy. Methods & clinical development.