T. Bertorini

Development of a model‐based clinical trial simulation platform to optimize the design of clinical trials for Duchenne muscular dystrophy

A. Pestronk, A. Nicorici, J. Florence, 2021, CPT: pharmacometrics & systems pharmacology.

Characteristics of the cardiac hypertrophy in Friedreich's ataxia.

J. Gottdiener, B. Maron, R. J. Hawley, 1982, American heart journal.

Psychophysiological Parameters of Migraine and Muscle‐Contraction Headaches

K. Lichstein, P. Hoon, J. Amberson, 1991, Headache.

Findings from the Longitudinal CINRG Becker Natural History Study

G. Manousakis, M. Wicklund, E. Henricson, 2023, Journal of neuromuscular diseases.