Renee Cooksley

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

S. S. St Martin, Yolanda Santiago, M. Holmes, 2018, Molecular therapy : the journal of the American Society of Gene Therapy.

Neurocognitive and neuropsychiatric phenotypes associated with the mutation L238Q of the α-L-iduronidase gene in Hurler-Scheie syndrome.

Alia Ahmed, C. Whitley, S. Cagle, 2014, Molecular genetics and metabolism.