Alex J. Klein

Mini-PCDH15 gene therapy rescues hearing in a mouse model of Usher syndrome type 1F

D. Corey, M. Sotomayor, K. Booth, 2023, Nature communications.

AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear

D. Corey, Yaqiao Li, C. Maguire, 2021, Molecular therapy. Methods & clinical development.