Miguel M. Lopes

Isolation of Biologically Active Extracellular Vesicles-Associated AAVs for Gene Delivery to the Brain by Size Exclusion Chromatography

M. Santana, L. Gaspar, Sonia P Duarte, 2023, bioRxiv.

A new protocol for whole-brain biodistribution analysis of AAVs by tissue clearing, light-sheet microscopy and semi-automated spatial quantification.

L. Pereira de Almeida, J. Paysan, J. Rino, 2022, Gene therapy.

ULK overexpression mitigates motor deficits and neuropathology in mouse models of Machado-Joseph disease.

I. M. Martins, L. Pereira de Almeida, C. Nóbrega, 2021, Molecular therapy : the journal of the American Society of Gene Therapy.

Protocol for the Characterization of the Cytosine-Adenine-Guanine Tract and Flanking Polymorphisms in Machado-Joseph Disease

L. Pereira de Almeida, C. Januário, N. Mendonça, 2020, The Journal of Molecular Diagnostics.

Protocol for the Characterization of the CAG Tract and Flanking Polymorphisms in Machado-Joseph Disease: Impact on Diagnosis and Development of Gene-Based Therapies.

L. Pereira de Almeida, C. Januário, N. Mendonça, 2020, The Journal of molecular diagnostics : JMD.

miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3

Valérie Ferreira, L. Pereira de Almeida, Sonia P Duarte, 2021, Nucleic acid therapeutics.