Janine A. Gilkes

Mucopolysaccharidosis III (Sanfilippo Syndrome)- disease presentation and experimental therapies.

C. Heldermon, Janine A Gilkes, Janine A. Gilkes, 2014, Pediatric endocrinology reviews : PER.

Site-specific modifications to AAV8 capsid yields enhanced brain transduction in the neonatal MPS IIIB mouse

S. Boye, R. Mandel, C. Heldermon, 2020, Gene Therapy.

The renin–angiotensin system and prevention of age-related functional decline: where are we now?

C. Simon, T. Buford, C. Carter, 2015, AGE.

Assessment of free fatty acids and cholesteryl esters delivered in liposomes as novel class of antibiotic

S. Chiang, S. Kosina, E. Porter, 2016, BMC Research Notes.

Mucopolysaccharidosis IIIB confers enhanced neonatal intracranial transduction by AAV8 but not by 5, 9 or rh10

C. Heldermon, J. Gilkes, M. D. Bloom, 2015, Gene Therapy.

Preferred transduction with AAV8 and AAV9 via thalamic administration in the MPS IIIB model: A comparison of four rAAV serotypes

C. Heldermon, J. Gilkes, M. D. Bloom, 2015, Molecular genetics and metabolism reports.