Yari Giménez

TALEN mediated gene editing in a mouse model of Fanconi anemia

J. Surrallés, S. Rodríguez-Perales, T. Cathomen, 2020, Scientific Reports.

Therapeutic gene editing in hematopoietic progenitor cells from a mouse model of Fanconi anemia

J. Surrallés, S. Rodríguez-Perales, T. Cathomen, 2018, bioRxiv.

Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia

J. Soulier, J. Surrallés, R. Yañez, 2019, Nature Medicine.

Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes

J. Soulier, J. Surrallés, M. Bogliolo, 2021, Molecular therapy. Methods & clinical development.

Next-generation Sequencing in Bone Marrow Failure Syndromes and Isolated Cytopenias: Experience of the Spanish Network on Bone Marrow Failure Syndromes

J. Surrallés, P. Lapunzina, M. Bogliolo, 2021, HemaSphere.

TALEN mediated gene editing in a mouse model of Fanconi anemia

J. Surrallés, S. Rodríguez-Perales, T. Cathomen, 2020, Scientific Reports.

Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia

L. D. Da Costa, J. Segovia, B. Strahm, 2024, JCI insight.