David D. Fuller

Current avenues of gene therapy in Pompe disease

B. Byrne, M. Corti, Matthew Gentry, 2023, Current opinion in neurology.

Advancements in AAV-mediated Gene Therapy for Pompe Disease

B. Byrne, N. Raben, N. Clément, 2019, Journal of neuromuscular diseases.

Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in Children Affected by Pompe Disease.

T. Conlon, B. Byrne, I. Tuna, 2017, Human gene therapy. Clinical development.