Guillermo Chacaltana

Rescue of blood coagulation Factor VIII exon-16 mis-splicing by antisense oligonucleotides

Michael D. Stone, J. Sanford, Catherine Oh, 2023, bioRxiv.

An intronic RNA element modulates Factor VIII exon-16 splicing

Catherine Oh, Nicholas M. Forino, Victor Tse, 2023, Nucleic acids research.