George Dickson

发表

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

I. Graham, K. Bushby, F. Muntoni, 2009, The Lancet Neurology.

Gene Therapy for Duchenne Muscular Dystrophy

George Dickson, Nertiyan Elangkovan, 2021, Journal of neuromuscular diseases.

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

J. Bourke, K. Bushby, F. Muntoni, 2011, The Lancet.

Mini- and full-length dystrophin gene transfer induces the recovery of nitric oxide synthase at the sarcolemma of mdx4cv skeletal muscle fibers

G. Dickson, B. Jasmin, John A. Lunde, 1998, Gene Therapy.

Intramuscular injection of a plasmid vector expressing human apolipoprotein E limits progression of xanthoma and aortic atheroma in apoE-deficient mice.

D. Riddell, A. Tagalakis, M. Dunckley, 2000, Human molecular genetics.

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

V. Arechavala-Gomeza, S. Çırak, M. Guglieri, 2011, The Lancet.

Expression of human full-length and minidystrophin in transgenic mdx mice: implications for gene therapy of Duchenne muscular dystrophy.

Y. Sunada, K. Wells, George Dickson, 1995, Human molecular genetics.

Modulation of pre-mRNA splicing in the Duchenne muscular dystrophy gene.

M. Dunckley, George Dickson, Ian C. Eperon, 1996, Biochemical Society transactions.

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

I. Graham, K. Bushby, L. Popplewell, 2009, The Lancet Neurology.

PABPN1 gene therapy for oculopharyngeal muscular dystrophy

S. Blumen, K. Mamchaoui, G. Dickson, 2017, Nature Communications.

Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and 1 skeletal muscles in the DMD mdx rat model 2 3

L. Popplewell, T. Larcher, S. Remy, 2021 .

Genetic correction of dystrophin deficiency and skeletal muscle remodeling in adult MDX mouse via transplantation of retroviral producer cells.

A. Fassati, F. Walsh, G. Dickson, 1997, The Journal of clinical investigation.