Anne M. Connolly

Natural history of infantile‐onset spinal muscular atrophy

Craig McDonald, Christopher S Coffey, Seward B Rutkove, 2017, Annals of neurology.

Onasemnogene Abeparvovec Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update

R. Finkel, T. Crawford, M. Schultz, 2019, Neuropediatrics.

Baseline results of the NeuroNEXT spinal muscular atrophy infant biomarker study

R. Finkel, M. Cudkowicz, S. Rutkove, 2016, Annals of clinical and translational neurology.