Cathleen M. Lutz

Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of Multiple Sulfatase Deficiency

A. Guerra, Parith Wongkittichote, Maximiliano Presa, 2024, bioRxiv.

Into the Wild: A novel wild-derived inbred strain resource expands the genomic and phenotypic diversity of laboratory mouse models

M. Phifer-Rixey, R. Lawal, B. Dumont, 2024, PLoS Genetics.

Efficient in vivo neuronal genome editing in the mouse brain using nanocapsules containing CRISPR-Cas9 ribonucleoproteins

M. Emborg, Ruosen Xie, Viktoriya Bondarenko, 2022, bioRxiv.

Expression of ALS-PFN1 impairs vesicular degradation in iPSC-derived microglia

D. A. Bosco, J. Landers, F. Massi, 2024, Nature communications.