A. Connolly

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

G. Acsadi, M. Scoto, E. Finanger, 2024, The Lancet Neurology.

Longitudinal pulmonary function testing outcome measures in Duchenne muscular dystrophy: Long-term natural history with and without glucocorticoids

A. Pestronk, R. Abresch, J. Bodensteiner, 2017, Neuromuscular Disorders.

Findings from the Longitudinal CINRG Becker Natural History Study

G. Manousakis, M. Wicklund, E. Henricson, 2023, Journal of neuromuscular diseases.