Daniel O’Reilly

Challenges of Assessing Exon 53 Skipping of the Human DMD Transcript with Locked Nucleic Acid-Modified Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy

Annemieke Aartsma-Rus, M. Damha, M. van Putten, 2023, Nucleic acid therapeutics.

A programmable dual-targeting siRNA scaffold supports potent two-gene modulation in the central nervous system

E. Sapp, Dimas Echeverria, Ashley Summers, 2024, Nucleic acids research.