Enabling redosing of AAV by immune management in Pompe disease: Preclinical to clinical studies
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B. Byrne | R. Herzog | N. Clément | M. Corti | A. Tarantal | B. Cleaver | Janet M. Benson | Genscheng Wang
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B. Byrne | R. Herzog | N. Clément | M. Corti | A. Tarantal | B. Cleaver | Janet M. Benson | Genscheng Wang