AAV-mediated transcription factor EB (TFEB) gene delivery ameliorates muscle pathology and function in the murine model of Pompe Disease
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A. Ballabio | R. Polishchuk | G. Diez-Roux | G. Parenti | F. Iacobellis | E. De Leonibus | A. Auricchio | F. Gatto | E. Polishchuk | E. Nusco | B. Rossi | A. Carrella | F. Alvino | A. Tarallo
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