Naked Plasmid DNA-Based α-Galactosidase A Gene Transfer Partially Reduces Systemic Accumulation of Globotriaosylceramide in Fabry Mice
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J. Miyazaki | A. Kulkarni | S. Ishii | F. Gejyo | H. Maruyama | Toru Kono | G. Nakamura | Masaaki Shimotori | S. Kameda