Recommendations on the diagnosis and management of Niemann-Pick disease type C.
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M. Baumgartner | F. Sedel | M. Patterson | M. Topcu | B. Bembi | M. Pineda | H. Widner | A. Covanis | T. Levade | M. Vanier | E. Mengel | J. E. Wraith | F. Wijburg | M. Topçu | J. Wraith
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