AAV-mediated transcription factor EB (TFEB) gene delivery ameliorates muscle pathology and function in the murine model of Pompe Disease
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Francesca Iacobellis | Andrea Ballabio | A. Ballabio | R. Polishchuk | G. Diez-Roux | G. Parenti | F. Iacobellis | E. De Leonibus | A. Auricchio | F. Gatto | E. Polishchuk | Francesca Gatto | Barbara Rossi | Antonietta Tarallo | Elena Polishchuk | Roman Polishchuk | Alessandra Carrella | Edoardo Nusco | Filomena Grazia Alvino | Elvira De Leonibus | Alberto Auricchio | Graciana Diez-Roux | Giancarlo Parenti | E. Nusco | B. Rossi | A. Carrella | F. Alvino | A. Tarallo | Francesca Gatto | Francesca Iacobellis | Antonietta Tarallo
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