Hematopoietic Stem Cell Transplantation in PNH

[1]  N. Geller,et al.  Long-term outcome of fludarabine-based reduced-intensity allogeneic hematopoietic cell transplantation for debilitating paroxysmal nocturnal hemoglobinuria. , 2014, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[2]  D. Morillo,et al.  Paroxysmal nocturnal hemoglobinuria: a single Spanish center’s experience over the last 40 yr , 2014, European journal of haematology.

[3]  A. Teigler‐Schlegel,et al.  Hematopoietic stem cell transplantation in children and young adults with secondary myelodysplastic syndrome and acute myelogenous leukemia after aplastic anemia. , 2014, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[4]  G. Socié Allogeneic BM transplantation for the treatment of aplastic anemia: current results and expanding donor possibilities. , 2013, Hematology. American Society of Hematology. Education Program.

[5]  N. Young,et al.  Current concepts in the pathophysiology and treatment of aplastic anemia. , 2013, Hematology. American Society of Hematology. Education Program.

[6]  A. Kulasekararaj,et al.  Management of the refractory aplastic anemia patient: what are the options? , 2013, Blood.

[7]  D. Blaise,et al.  Allogeneic stem cell transplantation in paroxysmal nocturnal hemoglobinuria , 2012, Haematologica.

[8]  T. Matsui,et al.  Strategy for bone marrow transplantation in eculizumab-treated paroxysmal nocturnal hemoglobinuria , 2011, International journal of hematology.

[9]  W. Gregory,et al.  Long-term treatment with eculizumab in paroxysmal nocturnal hemoglobinuria: sustained efficacy and improved survival. , 2010, Blood.

[10]  J. Kurtzberg,et al.  Influence of nucleated cell dose on overall survival of unrelated cord blood transplantation for patients with severe acquired aplastic anemia: a study by eurocord and the aplastic anemia working party of the European group for blood and marrow transplantation. , 2011, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[11]  A. Risitano,et al.  Hematopoietic stem cell transplantation for paroxysmal nocturnal hemoglobinuria: long-term results of a retrospective study on behalf of the Gruppo Italiano Trapianto Midollo Osseo (GITMO) , 2010, Haematologica.

[12]  M. Mohty,et al.  Paroxysmal nocturnal hemoglobinuria: natural history of disease subcategories. , 2008, Blood.

[13]  Richard J. Jones,et al.  Reduced intensity HLA-haploidentical BMT with post transplantation cyclophosphamide in nonmalignant hematologic diseases , 2008, Bone Marrow Transplantation.

[14]  N. Young,et al.  Multicenter phase 3 study of the complement inhibitor eculizumab for the treatment of patients with paroxysmal nocturnal hemoglobinuria. , 2008, Blood.

[15]  N. Young,et al.  The complement inhibitor eculizumab in paroxysmal nocturnal hemoglobinuria. , 2006, The New England journal of medicine.

[16]  M. Wojciechowska,et al.  First two successful unrelated donor bone marrow transplantations for paroxysmal nocturnal hemoglobinuria in Poland. , 2005, Annals of transplantation.

[17]  J. P. McCoy,et al.  In vitro and in vivo evidence of PNH cell sensitivity to immune attack after nonmyeloablative allogeneic hematopoietic cell transplantation. , 2004, Blood.

[18]  S. Richards,et al.  Effect of eculizumab on hemolysis and transfusion requirements in patients with paroxysmal nocturnal hemoglobinuria. , 2004, The New England journal of medicine.

[19]  R. Storb,et al.  Hematopoietic cell transplantation from related and unrelated donors after minimal conditioning as a curative treatment modality for severe paroxysmal nocturnal hemoglobinuria. , 2003, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[20]  Je-Hwan Lee,et al.  Allogeneic hematopoietic cell transplantation for paroxysmal nocturnal hemoglobinuria , 2003, European journal of haematology.

[21]  L. Isola,et al.  Low-dose total body irradiation, fludarabine, and antithymocyte globulin conditioning for nonmyeloablative allogeneic transplantation. , 2003, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[22]  C. Niemeyer,et al.  Stem cell transplantation for paroxysmal nocturnal haemoglobinuria in childhood. , 2002, British journal of haematology.

[23]  Y. Kim,et al.  Conditioning with high-dose cyclophosphamide may not be sufficient to provide a long-term remission of paroxysmal nocturnal hemoglobinuria following syngeneic peripheral blood stem cell transplantation , 2001, Bone Marrow Transplantation.

[24]  S. Mineishi,et al.  Successful application of nonmyeloablative transplantation for paroxysmal nocturnal hemoglobinuria. , 2001, Experimental hematology.

[25]  E. Horwitz,et al.  Successful unrelated donor bone marrow transplantation for paroxysmal nocturnal hemoglobinuria , 2001, Bone Marrow Transplantation.

[26]  F. Benvenuto,et al.  Bone marrow transplantation for paroxysmal nocturnal hemoglobinuria. , 2000, Haematologica.

[27]  M. Kletzel,et al.  Hematopoietic stem‐cell transplantation using unrelated cord‐blood versus matched sibling marrow in pediatric bone marrow failure syndrome: One center’s experience , 1999, Pediatric transplantation.

[28]  H. Esperou,et al.  Bone marrow transplantation for paroxysmal nocturnal haemoglobinuria , 1999, British journal of haematology.

[29]  L. Luzzatto,et al.  Bone marrow transplants for paroxysmal nocturnal haemoglobinuria , 1999, British journal of haematology.

[30]  H. Deeg,et al.  New somatic mutation in the PIG-A gene emerges at relapse of paroxysmal nocturnal hemoglobinuria. , 1998, Blood.

[31]  D. Fleming,et al.  Identical twin marrow transplantation for venous thrombosis in paroxysmal nocturnal hemoglobinuria; long-term complete remission as assessed by flow cytometry , 1998, Bone Marrow Transplantation.

[32]  J. Mary,et al.  Paroxysmal nocturnal haemoglobinuria: long-term follow-up and prognostic factors , 1996, The Lancet.

[33]  C. Wittwer,et al.  Syngeneic bone marrow transplantation without conditioning in a patient with paroxysmal nocturnal hemoglobinuria: in vivo evidence that the mutant stem cells have a survival advantage. , 1996, Blood.

[34]  C. Miller,et al.  Resolution of Budd‐Chiari syndrome following bone marrow transplantation for paroxysmal nocturnal haemoglobinuria , 1996, British journal of haematology.

[35]  S M Lewis,et al.  Natural history of paroxysmal nocturnal hemoglobinuria. , 1995, The New England journal of medicine.

[36]  R. Ribeiro,et al.  Late marrow allograft rejection following alpha-interferon therapy for hepatitis in a patient with paroxysmal nocturnal hemoglobinuria. , 1992, Bone marrow transplantation.

[37]  R. Storb,et al.  Marrow transplantation for paroxysmal nocturnal hemoglobinuria , 1992, American journal of hematology.

[38]  H. Gerhartz,et al.  Myeloablative conditioning for marrow transplantation in myelodysplastic syndromes and paroxysmal nocturnal haemoglobinuria. , 1989, Bone marrow transplantation.

[39]  S. Orkin,et al.  Bone marrow transplantation for paroxysmal nocturnal hemoglobinuria: eradication of the PNH clone and documentation of complete lymphohematopoietic engraftment , 1985 .

[40]  H. Deeg,et al.  Long-term survival after marrow transplantation for paroxysmal nocturnal hemoglobinuria with aplastic anemia. , 1984, Annals of internal medicine.

[41]  W. Wilmanns,et al.  [Bone marrow transplantation in adults in acute leukemia, aplastic anemia and paroxysmal nocturnal hemoglobinuria. Results of the Medical Clinic IIi of LMU (Ludwig-Maximilians University) Munich]. , 1983, Klinische Wochenschrift.

[42]  J. Adamson,et al.  Treatment of aplastic anemia by bone marrow transplantation in identical twins. , 1980, Blood.

[43]  R. Gale,et al.  CURE OF APLASTIC ANÆMIA IN PAROXYSMAL NOCTURNAL HÆMOGLOBINURIA BY MARROW TRANSFUSION FROM IDENTICAL TWIN: FAILURE OF PERIPHERAL-LEUCOCYTE TRANSFUSION TO CORRECT MARROW APLASIA , 1979, The Lancet.

[44]  R. Storb,et al.  Paroxysmal Nocturnal Hemoglobinuria and Marrow Failure Treated by Infusion of Marrow from an Identical Twin , 1976 .

[45]  P. Neiman,et al.  Paroxysmal Nocturnal Haemoglobinuria and Refractory Marrow Failure Treated by Marrow Transplantation , 1973, British journal of haematology.

[46]  R. Russell,et al.  Diphosphonates and Page's disease of bone. , 1971, Lancet.