Abnormal mannose-6-phosphate receptor trafficking impairs recombinant alpha-glucosidase uptake in Pompe disease fibroblasts
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G. Andria | G. Parenti | M. D. De Matteis | F. Donaudy | M. Vicinanza | E. Polishchuk | Caterina Porto | B. Rossi | M. Cardone | A. Tarallo | Francesca Donaudy