Efficacy and safety of lumacaftor and ivacaftor in patients aged 6-11 years with cystic fibrosis homozygous for F508del-CFTR: a randomised, placebo-controlled phase 3 trial.
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S. Stanojevic | D. Waltz | J. Davies | F. Ratjen | C. Milla | P. Robinson | G. Marigowda | S. Tian | Xiao-jing Huang | C. Hug | P. Robinson | Xiaohong Huang
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