Ataluren, a New Therapeutic for Alpha‐1 Antitrypsin‐Deficient Individuals with Nonsense Mutations
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M. Wormald | N. McElvaney | C. O’Dwyer | D. Kotton | S. Rowe | Andrew A. Wilson | E. Reeves | P. Hawkins | D. Dunlea | M. Alfares | Danielle M Dunlea | A. Wilson