Alpha-dystroglycan binding peptide A2G80-modified stealth liposomes as a muscle-targeting carrier for Duchenne muscular dystrophy.
暂无分享,去创建一个
Y. Hayashi | Shin‐ichi Hirashima | K. Nirasawa | Y. Negishi | Y. Kimura | M. Nomizu | N. Hamano | Fumihiko Katagiri | Y. Endo-Takahashi | Y. Kikkawa | T. Miura | K. Hamada | Sanae Sashida | Eri Sasaki | Takaaki Sakai | Masahiro Kawada | Akihiro Yoshida
[1] E. Olson,et al. Systemic nanoparticle delivery of CRISPR-Cas9 ribonucleoproteins for effective tissue specific genome editing , 2020, Nature Communications.
[2] M. Akaaboune,et al. The role of the dystrophin glycoprotein complex on the neuromuscular system , 2020, Neuroscience Letters.
[3] Y. Negishi,et al. Laminin-derived peptides: Applications in drug delivery systems for targeting. , 2019, Pharmacology & therapeutics.
[4] P. Cullis,et al. Lipid Nanoparticle Technology for Clinical Translation of siRNA Therapeutics. , 2019, Accounts of chemical research.
[5] P. Cullis,et al. A robust microfluidic technology and a new lipid composition for fabrication of curcumin-loaded liposomes: Effect on the anticancer activity and safety of cisplatin. , 2019, Molecular pharmaceutics.
[6] Jamie L. Marshall,et al. Stabilization of the cardiac sarcolemma by sarcospan rescues DMD-associated cardiomyopathy. , 2019, JCI insight.
[7] M. Ferrer,et al. Sunitinib promotes myogenic regeneration and mitigates disease progression in the mdx mouse model of Duchenne muscular dystrophy. , 2019, Human molecular genetics.
[8] P. Erbacher,et al. Non-Viral Vector Mediated Gene Delivery: the Outsider to Watch Out For in Gene Therapy , 2019, Cell and Gene Therapy Insights.
[9] S. Takeda,et al. Scavenger Receptor Class A1 Mediates Uptake of Morpholino Antisense Oligonucleotide into Dystrophic Skeletal Muscle , 2019, Molecular therapy. Nucleic acids.
[10] Y. Negishi,et al. Development of a Screening System for Targeting Carriers Using Peptide-Modified Liposomes and Tissue Sections. , 2018, Biological & pharmaceutical bulletin.
[11] J. Tucker,et al. Expression of glycosylated α‐dystroglycan in newborn skeletal and cardiac muscles of fukutin related protein (FKRP) mutant mice , 2017, Muscle & nerve.
[12] A. Fayssoil,et al. Cardiac Involvement Classification and Therapeutic Management in Patients with Duchenne Muscular Dystrophy , 2017, Journal of neuromuscular diseases.
[13] L. Zechiedrich,et al. Advances in Non-Viral DNA Vectors for Gene Therapy , 2017, Genes.
[14] Huali Chen,et al. PCM and TAT co-modified liposome with improved myocardium delivery: in vitro and in vivo evaluations , 2017, Drug delivery.
[15] S. Takeda,et al. Anti-inflammatory drugs for Duchenne muscular dystrophy: focus on skeletal muscle-releasing factors , 2016, Drug design, development and therapy.
[16] John M. Shelton,et al. Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy , 2016, Science.
[17] B. Byrne,et al. Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy , 2015, Annals of neurology.
[18] E. Hoffman,et al. The use of urinary and kidney SILAM proteomics to monitor kidney response to high dose morpholino oligonucleotides in the mdx mouse , 2015, Toxicology reports.
[19] Yvonne Perrie,et al. Microfluidic-controlled manufacture of liposomes for the solubilisation of a poorly water soluble drug. , 2015, International journal of pharmaceutics.
[20] T. Okazaki,et al. Inflammatory monocytes promote progression of Duchenne muscular dystrophy and can be therapeutically targeted via CCR2 , 2014, EMBO molecular medicine.
[21] J. Mendell,et al. Eteplirsen for the treatment of Duchenne muscular dystrophy , 2013, Annals of neurology.
[22] T. Yokota,et al. Antisense Therapy in Neurology , 2013, Journal of personalized medicine.
[23] Xiao Xiao,et al. Mouse models of fukutin-related protein mutations show a wide range of disease phenotypes , 2013, Human Genetics.
[24] Thomas Krucker,et al. Nonviral delivery of self-amplifying RNA vaccines , 2012, Proceedings of the National Academy of Sciences.
[25] Nathan M Belliveau,et al. Microfluidic Synthesis of Highly Potent Limit-size Lipid Nanoparticles for In Vivo Delivery of siRNA , 2012, Molecular therapy. Nucleic acids.
[26] Y. Barenholz. Doxil®--the first FDA-approved nano-drug: lessons learned. , 2012, Journal of controlled release : official journal of the Controlled Release Society.
[27] M. Hagiwara,et al. Chemical treatment enhances skipping of a mutated exon in the dystrophin gene , 2011, Nature communications.
[28] M. Nomizu,et al. Identification of alpha-dystroglycan binding sequences in the laminin alpha2 chain LG4-5 module. , 2010, Matrix biology : journal of the International Society for Matrix Biology.
[29] A. Nakamura,et al. Exon‐skipping therapy for Duchenne muscular dystrophy , 2009, Neuropathology : official journal of the Japanese Society of Neuropathology.
[30] Juan Li,et al. A muscle-targeting peptide displayed on AAV2 improves muscle tropism upon systemic delivery , 2009, Gene Therapy.
[31] P. Iversen,et al. Pharmacokinetics, biodistribution, stability and toxicity of a cell-penetrating peptide-morpholino oligomer conjugate. , 2007, Bioconjugate chemistry.
[32] Meenal Patel,et al. PTC124 targets genetic disorders caused by nonsense mutations , 2007, Nature.
[33] S. Peltz,et al. Safety, Tolerability, and Pharmacokinetics of PTC124, a Nonaminoglycoside Nonsense Mutation Suppressor, Following Single‐ and Multiple‐Dose Administration to Healthy Male and Female Adult Volunteers , 2007, Journal of clinical pharmacology.
[34] S. Futaki,et al. Cellular uptake and subsequent intracellular trafficking of R8-liposomes introduced at low temperature. , 2006, Biochimica et biophysica acta.
[35] S. Hirota,et al. Effects of mixed polyethyleneglycol modification on fixed aqueous layer thickness and antitumor activity of doxorubicin containing liposome. , 2002, International journal of pharmaceutics.
[36] R. Gaspar,et al. Use of the Post-Insertion Technique to Insert Peptide Ligands into Pre-Formed Stealth Liposomes with Retention of Binding Activity and Cytotoxicity , 2002, Pharmaceutical Research.
[37] M. Grounds,et al. Evans Blue Dye as an in vivo marker of myofibre damage: optimising parameters for detecting initial myofibre membrane permeability , 2002, Journal of anatomy.
[38] S. Futaki,et al. Arginine-rich Peptides , 2001, The Journal of Biological Chemistry.
[39] K. Campbell,et al. Molecular basis of muscular dystrophies , 2000, Muscle & nerve.
[40] S. Orcesi,et al. A multicenter, double‐blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy , 2000, Muscle & nerve.
[41] A. Nishikawa,et al. Visualization of dystrophic muscle fibers in mdx mouse by vital staining with Evans blue: evidence of apoptosis in dystrophin-deficient muscle. , 1995, Journal of biochemistry.
[42] A. Utani,et al. Identification of Cell Binding Sites in the Laminin α1 Chain Carboxyl-terminal Globular Domain by Systematic Screening of Synthetic Peptides (*) , 1995, The Journal of Biological Chemistry.
[43] A. Emery. Population frequencies of inherited neuromuscular diseases—A world survey , 1991, Neuromuscular Disorders.
[44] Eric P. Hoffman,et al. Dystrophin: The protein product of the duchenne muscular dystrophy locus , 1987, Cell.
[45] Giulia Anderluzzi,et al. Microfluidics based manufacture of liposomes simultaneously entrapping hydrophilic and lipophilic drugs. , 2016, International journal of pharmaceutics.