论文信息 - Clinical characteristics and genotypes in the ADVANCE baseline data set, a comprehensive cohort of US children and adolescents with Pompe disease - 字舞流文

Clinical characteristics and genotypes in the ADVANCE baseline data set, a comprehensive cohort of US children and adolescents with Pompe disease

D. Stockton | M. Gambello | N. Leslie | P. Tanpaiboon | L. Pena | J. Day | P. Kishnani | R. Hillman | J. Goldstein | Raymond Y. Wang | S. Sparks | D. Kronn | Yang Zhao | K. an Haack | S. Hahn | James B Gibson | James B. Gibson