Longitudinal In Vivo Monitoring of the CNS Demonstrates the Efficacy of Gene Therapy in a Sheep Model of CLN5 Batten Disease.
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T. Melzer | S. Gray | S. Hughes | L. Schoderboeck | G. Barrell | D. Palmer | M. Wellby | N. Mitchell | Katharina N. Russell | H. E. Wicky | Nadia L. Mitchell