论文信息 - Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice - 字舞流文

Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice

P. Sieving | Zhijian Wu | L. Wei | L. Ziccardi | D. Marangoni | P. Colosi | R. Bush | Kiran S Palyada | C. Vijayasarathy | S. Hiriyanna | Yong Zeng | J. Bartoe | M. Santos