Lineage- and stage-restricted lentiviral vectors for the gene therapy of chronic granulomatous disease
暂无分享,去创建一个
E. Laurenti | A. Trumpp | M. Wiznerowicz | D. Trono | A. Galy | S. Verp | I. Barde | S. Offner | A. Viornery | Sandra Offner | Elisa Laurenti | A. Trumpp | Sonia Verp | Isabelle Barde | Anne Galy | Didier Trono | Maciej Wiznerowicz
[1] Kathryn L. Parsley,et al. Biochemical correction of X-CGD by a novel chimeric promoter regulating high levels of transgene expression in myeloid cells. , 2011, Molecular therapy : the journal of the American Society of Gene Therapy.
[2] Jérôme Larghero,et al. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia , 2010, Nature.
[3] Hans Martin,et al. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease , 2010, Nature Medicine.
[4] Manfred Schmidt,et al. Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy , 2009, Science.
[5] A. Schambach,et al. Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors. , 2009, Molecular therapy : the journal of the American Society of Gene Therapy.
[6] Zhixiong Li,et al. Cell-intrinsic and vector-related properties cooperate to determine the incidence and consequences of insertional mutagenesis. , 2009, Molecular therapy : the journal of the American Society of Gene Therapy.
[7] M. Hansmann,et al. Resistance of mature T cells to oncogene transformation. , 2008, Blood.
[8] D. Duboule,et al. Genotypic Features of Lentivirus Transgenic Mice , 2008, Journal of Virology.
[9] C. Baum. Insertional mutagenesis in gene therapy and stem cell biology , 2007, Current opinion in hematology.
[10] O. Danos,et al. Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients , 2007, Gene Therapy.
[11] A. J. Valente,et al. Development of a synthetic promoter for macrophage gene therapy. , 2006, Human gene therapy.
[12] Clelia Di Serio,et al. Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration , 2006, Nature Biotechnology.
[13] Yang Du,et al. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1 , 2006, Nature Medicine.
[14] P. Opolon,et al. A lentiviral vector encoding the human Wiskott–Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice , 2005, Gene Therapy.
[15] F. Bushman,et al. Retroviral DNA Integration: ASLV, HIV, and MLV Show Distinct Target Site Preferences , 2004, PLoS biology.
[16] Cameron S. Osborne,et al. LMO2-Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1 , 2003, Science.
[17] T. Hawley,et al. Performance- and safety-enhanced lentiviral vectors containing the human interferon-β scaffold attachment region and the chicken β-globin insulator , 2003 .
[18] T. Hawley,et al. Performance- and safety-enhanced lentiviral vectors containing the human interferon-beta scaffold attachment region and the chicken beta-globin insulator. , 2003, Blood.
[19] L. Naldini,et al. Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in vivo. , 2002, Blood.
[20] J. Collinge,et al. Expression Pattern of a Mini Human PrP Gene Promoter in Transgenic Mice , 2002, Neurobiology of Disease.
[21] Félix Recillas-Targa,et al. Position-effect protection and enhancer blocking by the chicken β-globin insulator are separable activities , 2002, Proceedings of the National Academy of Sciences of the United States of America.
[22] Kathryn L. Parsley,et al. High-level transduction and gene expression in hematopoietic repopulating cells using a human imunodeficiency virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter , 2002 .
[23] David Baltimore,et al. Germline Transmission and Tissue-Specific Expression of Transgenes Delivered by Lentiviral Vectors , 2002, Science.
[24] Kathryn L. Parsley,et al. High-level transduction and gene expression in hematopoietic repopulating cells using a human immunodeficiency [correction of imunodeficiency] virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter. , 2002, Human gene therapy.
[25] Richard B. Johnston,et al. Chronic Granulomatous Disease: Report on a National Registry of 368 Patients , 2000, Medicine.
[26] T. Steinmann,et al. A Conserved Domain of the Arabidopsis GNOM Protein Mediates Subunit Interaction and Cyclophilin 5 Binding , 2000, Plant Cell.
[27] H. Malech. Progress in gene therapy for chronic granulomatous disease. , 1999, The Journal of infectious diseases.
[28] Luigi Naldini,et al. Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo , 1997, Nature Biotechnology.
[29] F. Gage,et al. In Vivo Gene Delivery and Stable Transduction of Nondividing Cells by a Lentiviral Vector , 1996, Science.
[30] T. Fleisher,et al. Flow cytometric analysis of the granulocyte respiratory burst: a comparison study of fluorescent probes. , 1995, Journal of immunological methods.
[31] David A. Williams,et al. Mouse model of X–linked chronic granulomatous disease, an inherited defect in phagocyte superoxide production , 1995, Nature Genetics.
[32] S. Orkin,et al. Targeting of transgene expression to monocyte/macrophages by the gp91-phox promoter and consequent histiocytic malignancies. , 1991, Proceedings of the National Academy of Sciences of the United States of America.
[33] R. Jaenisch,et al. A generic intron increases gene expression in transgenic mice , 1991, Molecular and cellular biology.
[34] J. Gauchat,et al. Superoxide-dependent nitroblue tetrazolium reduction and expression of cytochrome b-245 components by human tonsillar B lymphocytes and B cell lines. , 1989, Journal of immunology.
[35] A. Fauci,et al. B cell lines as models for inherited phagocytic diseases: abnormal superoxide generation in chronic granulomatous disease and giant granules in Chediak-Higashi syndrome. , 1984, Journal of immunology.