Liver-Directed AAV Gene Therapy for Gaucher Disease
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Rose M. Sheridan | R. Corbau | E. Chisari | J. Foley | A. Dane | A. Nathwani | Clément Cocita | J. Mcintosh | Carlos J. Miranda | M. Canavese | Azadeh Kia | Jalpa Pandya | Maria Portillo | J. Jeyakumar