论文信息 - Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial - 字舞流文

Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial

A. Buj-Bello | Jun Lee | E. James | A. Seferian | S. Rico | M. Noursalehi | F. Varfaj | Weston Miller | Fulvio Mavilio | A. R. Foley | James J. Dowling | Francesco Muntoni | Dimah N. Saade | Sarah B. Neuhaus | Alan H. Beggs | P. Shieh | N. Kuntz | W. Müller-Felber | Carsten G. Bönnemann | Laurent Servais | Barbara K. Smith | Astrid Blaschek | Lindsay N. Alfano | Martin K Childers | Tina Duong | Robert J. Graham | Minal S. Jain | Julie Coats | V. MacBean | Michael Murtagh | Cong Han | Michael W Lawlor | S. Prasad