Enzyme replacement therapy for mucopolysaccharidosis VI: a phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study.
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J. Wittes | R. Giugliani | J. E. Wraith | M. Newman | E. Teles | K. Berger | P. Harmatz | N. Guffon | M. Scarpa | M. Beck | I. Schwartz | E. Kakkis | S. Swiedler | Zi-Fan Yu | A. Lowe | Laila Arash | M. C. Miranda | M. C. S. Miranda | Zi‐Fan Yu
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