Activity of Transgene-Produced B-Domain Deleted Factor VIII in Human Plasma Following AAV5 Gene Therapy.
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K. Pasi | S. Rangarajan | G. Pierce | J. Pasi | S. Zoog | Jaydeep K. Srimani | C. Vettermann | A. Giermasz | S. Tiefenbacher | Terri M. Christianson | S. Rosén | E. Symington | Benjamin Kim | M. Robinson | Mei Huang | Donnie Mackenzie | Christian Vettermann | Stephen J. Zoog