Muscle overexpression of Klf15 via an AAV8-Spc5-12 construct does not provide benefits in spinal muscular atrophy mice
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Rafael J. Yáñez-Muñoz | M. Bowerman | P. Claus | R. Yáñez-Muñoz | Nina Ahlskog | A. Krueger | N. Ahlskog | S. Kubinski | Daniel Hayler