Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice
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S. Bunting | S. Fong | B. Carter | A. Bagri | C. O’Neill | L. Tsuruda | P. Colosi | G. Vehar | Lening Zhang | Britta Handyside | Choong-Ryoul Sihn | Lin Xie | Daniel Harmon | Sherry Bullens | R. Mahimkar | Shinong Long | Nicole Galicia | B. Yates | K. Sandza | S. Bullens | B. Handyside | L. Xie | Krystal Sandza
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