论文信息 - Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease - 字舞流文

Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease

A. Schambach | T. Maiwald | Zeenath Unnisa | Cecilia N. Barese | Christine E. Oborski | D. Clarke | Swaroopa Guda | N. P. van Til | Jeffrey W. Schindler | John K Yoon | Yildirim Dogan | Claudia Harper | C. Mason | Mary E. Jacobs | Richard Pfeifer | Niek P. van Til