Evidence for Efficacy and Safety of Lentiviral Mediated Gene Transfer in T Cells and CD34+ Cells from Wiskott-Aldrich Syndrome Patients.
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L. Naldini | L. Dupré | M. Roncarolo | A. Galy | A. Villa | A. Aiuti | F. Marangoni | S. Scaramuzza | A. Metin | S. Martino | S. Trifari