Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients
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O. Danos | L. Dupré | M. Roncarolo | A. Galy | A. Thrasher | A. Aiuti | A. Galy | S. Charrier | R. Eckenberg | F. Cattaneo | S. Scaramuzza | M. Blundell | L. Jeanson-Leh
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