Genomic safe harbors permit high β-globin transgene expression in thalassemia induced pluripotent stem cells
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Michel Sadelain | Frederic D Bushman | Manu Setty | Isabelle Riviere | Shoshannah L. Roth | Nirav Malani | F. Bushman | C. Leslie | A. Viale | M. Setty | M. Sadelain | Nirav Malani | E. Papapetrou | L. Studer | Gabsang Lee | P. Giardina | Agnes Viale | Lorenz Studer | K. Kadota | I. Rivière | Gabsang Lee | Laxmi MS Tirunagari | Kyuichi Kadota | Christina Leslie | Shoshannah L Roth | Patricia Giardina | Eirini P Papapetrou | Laxmi M S Tirunagari | N. Malani
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