Cerliponase alfa changes the natural history of children with neuronal ceroid lipofuscinosis type 2: The first French cohort.
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S. Auvin | I. Desguerre | A. Cano | B. Chabrol | D. Scavarda | S. Pichard | C. Hoebeke | Bastien Estublier
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S. Auvin | I. Desguerre | A. Cano | B. Chabrol | D. Scavarda | S. Pichard | C. Hoebeke | Bastien Estublier