Correction of cardiac abnormalities in fabry mice by direct intraventricular injection of a recombinant lentiviral vector that engineers expression of alpha-galactosidase A.
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J. Medin | K. Higuchi | Peter P. Liu | F. Dawood | M. Yoshimitsu | Manyin Chen | B. Ayach | V. Rasaiah | V. I. Rasaiah | Peter. P. Liu