论文信息 - Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study - 字舞流文

Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study

D. Stockton | M. Gambello | N. Leslie | P. Tanpaiboon | L. Pena | Yang Zhao | J. Day | P. Kishnani | R. Hillman | Loren D M Pena | Raymond Y. Wang | S. Sparks | On behalf of the Acmt Toxicology Investigators Consortium | D. Kronn | Yang Zhao | K. an Haack | S. Hahn | R. Shafi | James B Gibson | Catherine Wilson | Richard Hillman | James B. Gibson