Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/beta -microglobulin-/- repopulating mobilized human peripheral blood CD34+ cells.
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D. Bodine | H. Malech | E. Vanin | N. Whiting-Theobald | K. Holmes | S. Brenner | G. Linton | M. Horwitz | P. Kelly | A. M. Pilon | Mindy Anderson-Cohen
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